CureDuchenne Ventures Invests in MyoGene Bio and its AAV-Delivered CRISPR/Cas9 Gene Editing Approach
NEWPORT BEACH, Calif., May 11, 2023 /PRNewswire/ -- CureDuchenne Ventures announced funding for MyoGene Bio, LLC, a biotech company developing a novel gene editing therapy for Duchenne muscular dystrophy (DMD).
- NEWPORT BEACH, Calif., May 11, 2023 /PRNewswire/ -- CureDuchenne Ventures announced funding for MyoGene Bio, LLC, a biotech company developing a novel gene editing therapy for Duchenne muscular dystrophy (DMD).
- MyoGene will use this funding to advance development of MyoDys45-55, an AAV-delivered CRISPR/Cas9 gene editing approach that would be applicable to up to 50 percent of all DMD patients.
- The rationale for this approach comes from clinical cases of individuals naturally lacking this hotspot region between exons 45 and 55.
- "CureDuchenne Ventures has a long history of investing in gene therapy and gene editing research to treat DMD, and MyoGene Bio's approach is an excellent application of CRISPR/Cas9 technology to potentially address a large proportion – up to half – of DMD cases," said Debra Miller, founder and chief executive officer of CureDuchenne.